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Benzinga
Benzinga
Business
Vandana Singh

INSANE: Ionis pharmaceuticals reveals unprecedented results from rare neurological disease trial | Rare Historical Photos

Konskie,,Poland,-,ApIonis Pharmaceuticals

Ionis Pharmaceuticals, Inc. (NASDAQ:IONS) released topline results on Monday from the pivotal study of zilganersen in children and adults living with Alexander disease (AxD), a rare, progressive, and often fatal neurological condition.

The neurological disorder destroys the myelin sheath protecting nerve fibers, caused by a mutation in the GFAP gene.

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