Get all your news in one place.

100's of premium titles.
One app.

Start reading

Get all your news in one place.

100's of premium titles. One news app.

Start reading

REVEALED: 2 | Rare Historical Photos

Mother hails gene therapy treatment that restored daughter’s sight as ‘life-changing’

IN FULL

The Independent UK · Apr 22

Six-year-old girl has vision restored after first-of-its-kind NHS eye gene therapy

Saffie Sandford was diagnosed with the rare condition Leber’s Congenital Amaurosis (LCA) that affects vision in low light

The Independent UK · Apr 22

Six-year-old girl has sight restored thanks to life-changing eye gene therapy

Saffie Sandford had a first of its kind treatment for one of the genetic causes of her condition.

Evening Standard · Apr 22

From analysis to the latest developments in health,
read the most diverse news in one place.

Gene therapy improves hearing in 90% of patients with inherited deafness in largest trial of its kind

A new gene therapy tested in China has improved the hearing of 38 people who were born deaf due to mutations in a gene called OTOF.

LiveScience · Apr 22

‘Oscar of science’ awarded to team behind gene therapy that restores lost vision

Married couple Jean Bennett and Albert Maguire developed Luxturna, which helped a patient see their child’s face for the first time

The Guardian - UK · Apr 19

$3 million prize goes to duo whose research led to first sickle cell CRISPR therapy

Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a functional cure for the deadly blood disorders sickle cell disease and beta thalassemia.

LiveScience · Apr 19

Hearing Loss Breakthrough: The New Gene Therapy That Could Restore Hearing in Older Adults

Imagine being able to hear clearly again—without hearing aids, without implants, and without constant adjustments. That’s the promise behind a new wave of gene therapy...

Saving Advice · Apr 1

Read news from The Economist, FT, and more,
with one subscription

The Rise of Longevity Medicine: How Anti-Aging Clinics Promise Longer, Healthier Lives

Longevity medicine and anti aging clinics promise longer, healthier lives with biomarker testing, gene therapy, and personalized treatments.

Medical Daily · Mar 25

Forbes’ 250: Who are the 11 Indian Americans recently named America’s Greatest Innovators?

Eleven Indian Americans have been celebrated on Forbes' America's Greatest Innovators list, highlighting their transformative contributions across technology, biotech and infrastructure. These leaders, from AI pioneers to gene therapy developers, underscore the vital role of immigrant talent in shaping America's technological and economic future, inspiring a new generation of innovators.

The Times of India · Feb 27

UAE launches pioneering gene therapy to treat autism and rare brain disorders in children

The UAE has launched two gene therapy projects targeting the root causes of autism and rare brain disorders, marking a significant shift from symptom management to biological repair. Collaborating with global experts, these initiatives aim to enhance treatment effectiveness and safety for children with conditions like BPAN, paving the way…

The Times of India · Feb 21

As billionaires chase immortality, this startup cofounded by a Harvard genetics professor gets FDA approval for the first partial de-aging human trial

Life Biosciences will test its gene therapy designed to partially reset a cell’s age and potentially reverse vision loss in patients with glaucoma and NAION.

Fortune · Jan 30

Retired HGV driver undergoes heart bypass using gene therapy to reduce risks

The procedure aims to extend the lifespan of blood vessels used during the graft process in the surgery.

Evening Standard · Jan 7

From gene therapy breakthroughs to preventable disease outbreaks: The health trends that will shape 2026

Live Science's health channel editor makes predictions about the medical breakthroughs and public health shifts to come in 2026.

LiveScience · Dec 31, 2025

Groundbreaking UK gene therapy offers hope after progress of three-year-old

Oliver Chu from California first person to have the one-off treatment for Hunter syndrome

The Guardian - UK · Nov 24, 2025

Get all your
news in one place.

100's of premium titles.
One news app.

Medical Daily · Nov 19, 2025

Gene Editing Medicine and Personalized Medicine: Breakthroughs Driving Health Innovation Gene Therapy to Transform Care

Explore how gene editing medicine and personalized medicine future breakthroughs are revolutionizing health innovation gene therapy, offering precise, transformative treatments and medical breakthroughs for complex diseases.

The Independent UK · Nov 14, 2025

FDA adds strongest warning to Sarepta gene therapy linked to 2 patient deaths

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year

Medical Daily · Nov 12, 2025

Gene Therapy for Children With Rare 'Bubble Boy Disease' Proves Effective After Long-Term Follow-Up

A new gene therapy for children with the rare "Bubble Boy disease" proved to be effective following the results of long-term follow-ups.

Benzinga · Nov 10, 2025

Eli Lilly Expands Genetic Eye-Disease Focused Pipeline With MeiraGTx Gene Therapy Collaboration

MeiraGTx Holdings plc (NASDAQ:MGTX) stock is trading higher after the company inked a strategic collaboration in the area of ophthalmology with Eli Lilly and Co. (NYSE:LLY).

Get all your
news in one place.

100's of premium titles.
One news app.

Benzinga · Oct 24, 2025

Eli Lilly Bets Big On Eye Gene Therapy That Could End Repeat Injections

Eli Lilly and Company (NYSE:LLY) and Adverum Biotechnologies, Inc. (NASDAQ:ADVM) on Friday announced that they have entered into a definitive agreement under which Lilly will acquire Adverum Biotechnologies, including its lead product, Ixo-vec.

Euronews · Oct 16, 2025

Experimental gene therapy successfully treats dozens of children with rare fatal disorder

'These results are what we hoped for when we first began developing this approach,' one researcher said.

Benzinga · Oct 14, 2025

FDA Acceptance Of Rocket Pharmaceuticals' Lead Gene Therapy Application Reestablishes Momentum For Stock

On Tuesday, the U.S. Food and Drug Administration (FDA) accepted Rocket Pharmaceuticals, Inc.’s (NASDAQ:RCKT) resubmission of the Biologics License Application (BLA) for Kresladi (marnetegragene autotemcel; marne-cel), a lentiviral vector (LV)-based investigational gene therapy for severe Leukocyte Adhesion Deficiency-I (LAD-I).

Benzinga · Oct 13, 2025

Regeneron's Gene Therapy Shows Significant Gains In Genetic Hearing Loss

On Sunday, Regeneron Pharmaceuticals, Inc. (NASDAQ:REGN) unveiled updated data from its investigational gene therapy DB-OTO for profound genetic hearing loss caused by variants of the otoferlin (OTOF) gene.

The Conversation · Sep 29, 2025

A new treatment for Huntington’s disease is genuinely promising – but here’s why we still need caution

Imagine knowing in your 20s or 30s that you carry a gene which will cause your mind and body to slowly unravel. Huntington’s disease is inherited, relentless and fatal, and there is no cure. Families live with the certainty of decline stretching across generations.

The Conversation · Sep 29, 2025

New hope for Huntington’s families as gene therapy shows remarkable results

A company called uniQure has announced promising results from a trial of a new gene therapy for Huntington’s disease. The news has spread quickly through families affected by this condition, who have been desperately waiting for a treatment that can stop or slow down this devastating illness.

The Guardian - UK · Sep 26, 2025

Friday briefing: The Huntington’s treatment is a ray of light for victims of a brutal disease

In today’s newsletter: A gene therapy trial has successfully treated Huntington’s for the first time – one of several recent groundbreaking medical advances bringing hope in gloomy times

1 2 3 4 5

Coverage From

People

From analysis to the latest developments in health,
read the most diverse news in one place.

Organisations

the Food and Drug Administration

238 stories

Harvard Medical School

149 stories

the University of Glasgow

148 stories

the University of Pennsylvania

144 stories

the British Heart Foundation

135 stories

NHSGGC

130 stories

Read news from The Economist, FT, and more,
with one subscription

Topics

Places

Fourteen days free

Download the app

One app. One membership.
100+ trusted global sources.